No abstract available
Publication types
-
Research Support, Non-U.S. Gov't
MeSH terms
-
Cystic Fibrosis / genetics
-
Cystic Fibrosis / therapy*
-
Cystic Fibrosis Transmembrane Conductance Regulator / genetics*
-
Dependovirus / genetics*
-
Gene Editing*
-
Genetic Therapy / methods*
-
Genetic Vectors / administration & dosage*
-
Genetic Vectors / genetics
-
Humans
Substances
-
CFTR protein, human
-
Cystic Fibrosis Transmembrane Conductance Regulator