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J Pediatr. 2020 Aug:223:227-228. doi: 10.1016/j.jpeds.2020.04.069. Epub 2020 May 4.
No abstract available

Publication types

  • Letter
  • Comment

MeSH terms

  • Humans
  • Oligonucleotides*
  • Spinal Muscular Atrophies of Childhood*

Substances

  • Oligonucleotides
  • nusinersen