Target arm affinities determine preclinical efficacy and safety of anti-HER2/CD3 bispecific antibody

JCI Insight. 2020 Apr 9;5(7):e133757. doi: 10.1172/jci.insight.133757.

Abstract

Systemic cytokine release and on-target/off-tumor toxicity to normal tissues are the main adverse effects limiting the clinical utility of T cell-redirecting therapies. This study was designed to determine how binding affinity for CD3 and tumor target HER2 impact the efficacy and nonclinical safety of anti-HER2/CD3 T cell-dependent antibodies (TDBs). Affinity was found to be a major determinant for the overall tolerability. Higher affinity for CD3 associated with rapidly elevated peripheral cytokine concentrations, weight loss in mice, and poor tolerability in cynomolgus monkeys. A TDB with lower CD3 affinity was better tolerated in cynomolgus monkeys compared with a higher CD3-affinity TDB. In contrast to tolerability, T cell binding affinity had only limited impact on in vitro and in vivo antitumor activity. High affinity for HER2 was critical for the tumor-killing activity of anti-HER2/CD3 TDBs, but higher HER2 affinity also associated with a more severe toxicity profile, including cytokine release and damage to HER2-expressing tissues. The tolerability of the anti-HER2/CD3 was improved by implementing a dose-fractionation strategy. Fine-tuning the affinities for both the tumor target and CD3 is likely a valuable strategy for achieving maximal therapeutic index of CD3 bispecific antibodies.

Keywords: Oncology; T cells.

MeSH terms

  • Animals
  • Antibodies, Bispecific / chemistry
  • Antibodies, Bispecific / immunology*
  • Antibody Affinity*
  • Antineoplastic Agents, Immunological / chemistry
  • Antineoplastic Agents, Immunological / immunology*
  • CD3 Complex / chemistry
  • CHO Cells
  • Cricetulus
  • Drug Evaluation, Preclinical
  • Humans
  • Macaca fascicularis
  • Receptor, ErbB-2 / chemistry
  • Receptor, ErbB-2 / immunology*

Substances

  • Antibodies, Bispecific
  • Antineoplastic Agents, Immunological
  • CD3 Complex
  • ERBB2 protein, human
  • Receptor, ErbB-2