Response to everolimus of a progressive plexiform neurofibroma in Neurofibromatosis type 1

Pediatr Int. 2020 Jul;62(7):857-859. doi: 10.1111/ped.14183. Epub 2020 Jul 6.
No abstract available

Keywords: everolimus; mammalian target of rapamycin; neurofibromatosis type 1; plexiform neurofibroma; therapeutics.

Publication types

  • Case Reports

MeSH terms

  • Antineoplastic Agents / therapeutic use*
  • Child
  • Everolimus / therapeutic use*
  • Female
  • Humans
  • Magnetic Resonance Imaging / methods
  • Neurofibroma, Plexiform / complications
  • Neurofibroma, Plexiform / drug therapy*
  • Neurofibromatosis 1 / complications
  • Neurofibromatosis 1 / drug therapy*
  • TOR Serine-Threonine Kinases / metabolism
  • Treatment Outcome

Substances

  • Antineoplastic Agents
  • Everolimus
  • TOR Serine-Threonine Kinases