Challenges facing microRNA therapeutics for cystic fibrosis lung disease

Epigenomics. 2020 Feb;12(3):179-181. doi: 10.2217/epi-2019-0395. Epub 2020 Feb 3.
No abstract available

Keywords: adjunct therapy; cystic fibrosis; human CF models; lung delivery; miRNA.

Publication types

  • Editorial
  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Clinical Trials as Topic
  • Cystic Fibrosis / genetics*
  • Cystic Fibrosis / therapy*
  • Cystic Fibrosis Transmembrane Conductance Regulator / genetics
  • Genetic Therapy* / methods
  • Humans
  • MicroRNAs / therapeutic use*
  • Mutation
  • Treatment Outcome

Substances

  • CFTR protein, human
  • MicroRNAs
  • Cystic Fibrosis Transmembrane Conductance Regulator