Duchenne muscular dystrophy

BMJ. 2020 Jan 23:368:l7012. doi: 10.1136/bmj.l7012.
No abstract available

MeSH terms

  • Child
  • Creatine Kinase / blood
  • Delayed Diagnosis
  • Early Diagnosis
  • Female
  • Humans
  • Male
  • Muscular Dystrophy, Duchenne / complications
  • Muscular Dystrophy, Duchenne / diagnosis*
  • Muscular Dystrophy, Duchenne / drug therapy
  • Oxadiazoles / therapeutic use*
  • Patient Care Team
  • Quality of Life
  • Referral and Consultation
  • Sex Factors

Substances

  • Oxadiazoles
  • Creatine Kinase
  • ataluren