The road to biosimilars in rare diseases - ongoing lessons from Gaucher disease

Affiliations

• ¹ Hospital de Niños Ricardo Gutiérrez, Buenos Aires, Argentina.
• ² Departamento de Farmacología, Centro de Investigación y de Estudios Avanzados del Instituto Politécnico Nacional, Mexico City, Mexico.
• ³ Division of Hematology, Department of Internal Medicine, Istanbul University-Cerrahpasa, Cerrahpasa Faculty of Medicine, Istanbul, Turkey.
• ⁴ Departamento de Oncohematología, Henry Moore Institute, Buenos Aires, Argentina.
• ⁵ Centro Latino Americano de Pesquisa em Biológicos, São Paulo, Brazil.
• ⁶ Department of Clinical Pharmacology and Therapeutics, Seoul National University College of Medicine and Hospital, Graduate School of Convergence Science and Technology, Seoul National University, South Korea.
• ⁷ Tareev Clinic of Internal Diseases, Sechenov First Moscow State Medical University, Moscow, Russia.
• ⁸ Genetic Research Center in Non-Communicable Disease, Zahedan University of Medical Sciences, Zahedan, Iran.
• ⁹ Hematology Clinic, Clalit services, Nazareth Towers, Israel.
• ¹⁰ International Gaucher Alliance, Dursley, UK.
• ¹¹ Departamento de Farmacologia y Toxicologia, Facultad de Medicina, Universidad de Antioquia, Medellín, Colombia.
• ¹² Global Medical Affairs, Sanofi Genzyme, Cambridge, Massachusetts.
• ¹³ Department of Medicine, Yale University School of Medicine, New Haven, Connecticut.