Reply to Chacko et al.: Limited Assessment of Respiratory Muscle Response to Nusinersen Treatment in Infants with Spinal Muscular Atrophy

Am J Respir Crit Care Med. 2020 Mar 1;201(5):624-626. doi: 10.1164/rccm.201910-2022LE.
No abstract available

Publication types

  • Letter
  • Comment

MeSH terms

  • Humans
  • Infant
  • Muscular Atrophy, Spinal*
  • Oligonucleotides
  • Respiratory Muscles
  • Spinal Muscular Atrophies of Childhood*

Substances

  • Oligonucleotides
  • nusinersen