Effect of Nusinersen on Respiratory Muscle Function in Different Subtypes of Type 1 Spinal Muscular Atrophy

Am J Respir Crit Care Med. 2019 Dec 15;200(12):1547-1550. doi: 10.1164/rccm.201906-1175LE.
No abstract available

Publication types

  • Letter

MeSH terms

  • Child, Preschool
  • Cohort Studies
  • Female
  • Humans
  • Infant
  • Male
  • Oligonucleotides / therapeutic use*
  • Respiratory Muscles / drug effects*
  • Respiratory Muscles / physiopathology
  • Spinal Muscular Atrophies of Childhood / drug therapy*
  • Spinal Muscular Atrophies of Childhood / physiopathology*

Substances

  • Oligonucleotides
  • nusinersen