No abstract available
MeSH terms
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Child, Preschool
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Cohort Studies
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Female
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Humans
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Infant
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Male
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Oligonucleotides / therapeutic use*
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Respiratory Muscles / drug effects*
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Respiratory Muscles / physiopathology
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Spinal Muscular Atrophies of Childhood / drug therapy*
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Spinal Muscular Atrophies of Childhood / physiopathology*
Substances
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Oligonucleotides
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nusinersen