[A case of SBBYSS syndrome caused by KAT6B gene variant]

Zhonghua Yi Xue Yi Chuan Xue Za Zhi. 2019 Jul 10;36(7):727-730. doi: 10.3760/cma.j.issn.1003-9406.2019.07.018.
[Article in Chinese]

Abstract

Objective: To analyze the clinical and molecular genetics features of a family affected with Say-Barber-Biesecker-Young-Simpson syndrome (SBBYSS).

Methods: High-throughput sequencing was used to detect copy number variations (CNVs) and pathogenic variant within the whole exome of the affected child.

Results: No pathogenic CNV was found in the child, while exome sequencing identified a heterozygous c.3367_c.3370delAGAA (p.Arg1123Argfs*6) frameshifting variant in the exon 16 of the KAT6B gene. The same variant was not found in either parent.

Conclusion: The c.3367_c.3370delAGAA (p.R1123Rfs*6) probably underlies the disease in the affected child. Above finding has facilitated genetic counseling and prenatal diagnosis for the family.

MeSH terms

  • Blepharophimosis / genetics*
  • Child
  • Congenital Hypothyroidism / genetics*
  • DNA Copy Number Variations*
  • Facies
  • Female
  • Heart Defects, Congenital / genetics*
  • Histone Acetyltransferases / genetics*
  • Humans
  • Intellectual Disability / genetics*
  • Joint Instability / genetics*
  • Mutation
  • Phenotype
  • Pregnancy

Substances

  • Histone Acetyltransferases
  • KAT6B protein, human

Supplementary concepts

  • Young Simpson syndrome