A systematic Cochrane Review of correctors (specific therapies for class II CFTR mutations) for cystic fibrosis

Paediatr Respir Rev. 2019 Apr:30:25-26. doi: 10.1016/j.prrv.2019.01.003. Epub 2019 Feb 7.
No abstract available

Publication types

  • Systematic Review

MeSH terms

  • Aminophenols / therapeutic use*
  • Aminopyridines / therapeutic use*
  • Benzodioxoles / therapeutic use*
  • Cystic Fibrosis / drug therapy*
  • Cystic Fibrosis / genetics
  • Cystic Fibrosis Transmembrane Conductance Regulator / genetics
  • Drug Therapy, Combination
  • Humans
  • Indoles / therapeutic use*
  • Quinolones / therapeutic use*
  • Treatment Outcome

Substances

  • Aminophenols
  • Aminopyridines
  • Benzodioxoles
  • CFTR protein, human
  • Indoles
  • Quinolones
  • tezacaftor
  • Cystic Fibrosis Transmembrane Conductance Regulator
  • ivacaftor
  • lumacaftor