Micro-dystrophin Genes Bring Hope of an Effective Therapy for Duchenne Muscular Dystrophy

Mol Ther. 2019 Mar 6;27(3):486-488. doi: 10.1016/j.ymthe.2019.01.019. Epub 2019 Feb 12.

Authors

Kay E Davies¹, Simon Guiraud²

Affiliations

¹ MDUK Oxford Neuromuscular Centre, Department of Physiology, Anatomy and Genetics, University of Oxford, Oxford OX1 3PT, UK. Electronic address: kay.davies@dpag.ox.ac.uk.
² MDUK Oxford Neuromuscular Centre, Department of Physiology, Anatomy and Genetics, University of Oxford, Oxford OX1 3PT, UK.

No abstract available

Publication types

Comment

MeSH terms

Dystrophin / genetics*
Genetic Therapy
Humans
Muscular Dystrophy, Duchenne / genetics*

Substances

Dystrophin

Grants and funding

MR/N010698/1/MRC_/Medical Research Council/United Kingdom