Hemoglobinopathies in the Fetal Position

N Engl J Med. 2018 Oct 25;379(17):1675-1677. doi: 10.1056/NEJMcibr1809628.
No abstract available

MeSH terms

  • Anemia, Sickle Cell / drug therapy*
  • Anemia, Sickle Cell / genetics
  • CRISPR-Cas Systems
  • Carrier Proteins / genetics
  • Erythroid Cells / metabolism
  • Fetal Hemoglobin / genetics*
  • Gene Expression Regulation*
  • Humans
  • Molecular Targeted Therapy
  • eIF-2 Kinase / antagonists & inhibitors*
  • eIF-2 Kinase / genetics
  • eIF-2 Kinase / metabolism

Substances

  • Carrier Proteins
  • Fetal Hemoglobin
  • EIF2AK1 protein, human
  • eIF-2 Kinase