No abstract available
Publication types
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Letter
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Research Support, N.I.H., Extramural
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Research Support, Non-U.S. Gov't
MeSH terms
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Codon, Nonsense / genetics*
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Humans
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Middle Aged
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Oxadiazoles / therapeutic use*
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alpha 1-Antitrypsin / metabolism
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alpha 1-Antitrypsin Deficiency / drug therapy*
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alpha 1-Antitrypsin Deficiency / genetics
Substances
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Codon, Nonsense
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Oxadiazoles
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alpha 1-Antitrypsin
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ataluren