Accelerating evidence gathering and approval of precision medicine therapies: the FDA takes aim at rare mutations

Genet Med. 2019 Mar;21(3):542-544. doi: 10.1038/s41436-018-0099-0. Epub 2018 Jul 10.

Amalia M Issa^{1

2

3}, Adrian Thorogood⁴, Yann Joly⁴, Bartha M Knoppers⁴

¹ Personalized Medicine & Targeted Therapeutics, University of the Sciences in Philadelphia, Philadelphia, Pennsylvania, USA. amalia.issa2@mcgill.ca.
² Pharmaceutical Sciences; Health Policy & Public Health, University of the Sciences in Philadelphia, Philadelphia, Pennsylvania, USA. amalia.issa2@mcgill.ca.
³ Centre of Genomics and Policy, McGill University, Montreal, Quebec, Canada. amalia.issa2@mcgill.ca.
⁴ Centre of Genomics and Policy, McGill University, Montreal, Quebec, Canada.

No abstract available

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