No abstract available
MeSH terms
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Clinical Trials as Topic
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Drug Approval
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Dystrophin / drug effects*
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Dystrophin / metabolism*
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Humans
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Morpholinos / administration & dosage
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Morpholinos / pharmacology*
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Muscular Dystrophy, Duchenne / drug therapy*
Substances
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Dystrophin
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Morpholinos
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eteplirsen