[Place of the expert patient in the R&D process in the field of rare diseases]

MeSH terms

• Adolescent
• Biomedical Research / organization & administration*
• Child
• Cooperative Behavior
• Expert Testimony*
• Female
• Humans
• Mucopolysaccharidosis III / pathology
• Mucopolysaccharidosis III / therapy
• Patient Advocacy / standards
• Patient Education as Topic*
• Patient Participation
• Professional-Patient Relations*
• Rare Diseases / pathology
• Rare Diseases / therapy*
• Role
• Therapies, Investigational / trends