Five-aminolevulinic acid: New approach for congenital sideroblastic anemia

Pediatr Int. 2018 May;60(5):496-497. doi: 10.1111/ped.13558.
No abstract available

Keywords: 5-aminolevulinate synthase 2; 5-aminolevulinic acid; congenital sideroblastic anemia; pharmacokinetics.

Publication types

  • Case Reports

MeSH terms

  • Aminolevulinic Acid / therapeutic use*
  • Anemia, Sideroblastic / congenital
  • Anemia, Sideroblastic / diagnosis
  • Anemia, Sideroblastic / drug therapy*
  • Hematinics / therapeutic use*
  • Humans
  • Male
  • Young Adult

Substances

  • Hematinics
  • Aminolevulinic Acid