Advanced therapies in rare diseases: the example of spinal muscular atrophy
Med Clin (Barc). 2018 Oct 12;151(7):275-277.
doi: 10.1016/j.medcli.2018.03.001.
Epub 2018 Apr 21.
[Article in
English,
Spanish]
Affiliation
- 1 Área de Genética Clínica y Molecular-Unidad Funcional de Enfermedades Raras, Grupo de Medicina Genética VHIR, CIBERER, Hospital Universitario Vall d'Hebron, Barcelona, España. Electronic address: etizzano@vhebron.net.
No abstract available
Publication types
-
Editorial
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Research Support, Non-U.S. Gov't
MeSH terms
-
Child
-
Child, Preschool
-
Humans
-
Infant
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Muscular Atrophy, Spinal / drug therapy*
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Rare Diseases / drug therapy*