A 5-center experience with intrathecal administration of nusinersen in SMA1 in Italy letter to the editor of european journal of pediatric neurology regarding the manuscript "single-center experience with intrathecal administration of nusinersen in children with spinal muscular atrophy type 1" written by pechmann and colleagues"

Eur J Paediatr Neurol. 2018 Jul;22(4):729-731. doi: 10.1016/j.ejpn.2018.02.004. Epub 2018 Feb 19.
No abstract available

Publication types

  • Letter
  • Comment

MeSH terms

  • Child
  • Humans
  • Italy
  • Muscular Atrophy, Spinal
  • Neurology
  • Oligonucleotides*
  • Spinal Muscular Atrophies of Childhood*

Substances

  • Oligonucleotides
  • nusinersen