Visualization of the therapeutic efficacy of a gene correction approach in Wilson's disease by laser-ablation inductively coupled mass spectrometry

J Hepatol. 2018 May;68(5):1088-1090. doi: 10.1016/j.jhep.2017.12.022. Epub 2018 Jan 6.

¹ Gene Therapy and Regulation of Gene Expression Program, CIMA, Foundation for Applied Medical Research, University of Navarra, Pamplona, Spain; Instituto de Investigacion Sanitaria de Navarra (IDISNA), Pamplona, Spain.
² Institute of Molecular Pathobiochemistry, Experimental Gene Therapy and Clinical Chemistry (IFMPEGKC), RWTH University Hospital Aachen, D-52074 Aachen, Germany.
³ Gene Therapy and Regulation of Gene Expression Program, CIMA, Foundation for Applied Medical Research, University of Navarra, Pamplona, Spain; Instituto de Investigacion Sanitaria de Navarra (IDISNA), Pamplona, Spain; Vivet-Therapeutics, Pamplona, Spain. Electronic address: ggasegui@unav.es.
⁴ Institute of Molecular Pathobiochemistry, Experimental Gene Therapy and Clinical Chemistry (IFMPEGKC), RWTH University Hospital Aachen, D-52074 Aachen, Germany. Electronic address: rweiskirchen@ukaachen.de.

No abstract available

Keywords: ATP7B; Copper; Gene therapy; Metal; Wilson’s disease.

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