Hard targets for a second skeleton: therapeutic horizons for fibrodysplasia ossificans progressiva (FOP)

Expert Opin Orphan Drugs. 2017;5(4):291-294. doi: 10.1080/21678707.2017.1304211. Epub 2017 Mar 17.
No abstract available

Keywords: ACVR1; Activin A; bone morphogenetic protein receptors; fibrodysplasia ossificans progressiva; heterotopic endochondral ossification; hypoxia.