No abstract available
MeSH terms
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Animals
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Clinical Trials, Phase II as Topic
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Disease Models, Animal
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Distal Myopathies / drug therapy*
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Distal Myopathies / genetics
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Distal Myopathies / metabolism
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Distal Myopathies / pathology
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Drug Evaluation, Preclinical
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Humans
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Mice
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Mice, Transgenic
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N-Acetylneuraminic Acid / therapeutic use*
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Protein Processing, Post-Translational / drug effects
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Protein Processing, Post-Translational / physiology
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Research Design / standards
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Treatment Failure
Supplementary concepts
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Distal myopathy, Nonaka type