Rescuing Canavan disease: engineering the wrong cell at the right time

J Inherit Metab Dis. 2017 Sep;40(5):627-628. doi: 10.1007/s10545-017-0038-2. Epub 2017 Apr 3.
No abstract available

Keywords: ASPA Gene; Aspartoacylase; Canavan Disease; Myelin Layer; Turn Signal.

Publication types

  • Editorial
  • Comment

MeSH terms

  • Amidohydrolases
  • Aspartic Acid
  • Canavan Disease*
  • Humans
  • Myelin Sheath*

Substances

  • Aspartic Acid
  • Amidohydrolases