Minicircle-oriP-miR-31 as a Novel EBNA1-Specific miRNA Therapy Approach for Nasopharyngeal Carcinoma

Hum Gene Ther. 2017 May;28(5):415-427. doi: 10.1089/hum.2016.136. Epub 2016 Dec 29.

Abstract

MicroRNAs (miRNAs) are important post-transcriptional regulators that control cancer development and progression. However, the application of miRNA therapy in cancer has been hampered by a lack of an efficient and targeted delivery system. In our previous studies, an oriP promoter-based minicircle system successfully mediated targeted foreign gene expression in EBNA1-positive nasopharyngeal carcinoma (NPC). However, it remains to be evaluated whether this system can be applied for tumor miRNA therapy. miR-31-5p, a tumor suppressive miRNA involved in the tumorigenesis of EBV-positive NPC, was selected as the therapeutic miRNA to be transferred. In this work, we constructed a novel EBNA1-specific miRNA expression system, minicircle-oriP-miR-31. The results indicated that mc-oriP-miR-31 mediated selective miR-31-5p expression in EBNA1-positive NPC cells. Both the proliferation and migration of EBNA1-positive NPC cell lines were inhibited by mc-oriP-miR-31 treatment in vitro. Furthermore, mc-oriP-miR-31 treatment inhibited xenograft growth and lung metastasis in vivo. We also identified WDR5 as a novel miR-31-5p target. Knockdown of WDR5 inhibited NPC cell proliferation and migration and was associated with downregulation of Notch1. Reintroduction of WDR5 partially abrogated the suppressive effects induced by miR-31-5p. In conclusion, we demonstrate for the first time that targeted expression of miR-31-5p using a nonviral minicircle vector can serve as a novel approach for tumor miRNA therapy. Moreover, WDR5 may be a promising therapeutic target for NPC treatment.

Keywords: WDR5; miR-31-5p; minicircle; nasopharyngeal carcinoma; oriP.

MeSH terms

  • Animals
  • Carcinoma / genetics
  • Carcinoma / pathology
  • Carcinoma / therapy*
  • Cell Line, Tumor
  • Cell Movement / genetics
  • Cell Proliferation / genetics*
  • Epstein-Barr Virus Nuclear Antigens / genetics
  • Gene Expression Regulation, Neoplastic
  • Genetic Vectors / therapeutic use
  • Histone-Lysine N-Methyltransferase / genetics*
  • Humans
  • Intracellular Signaling Peptides and Proteins
  • Mice
  • MicroRNAs / genetics*
  • MicroRNAs / therapeutic use
  • Nasopharyngeal Carcinoma
  • Nasopharyngeal Neoplasms / genetics
  • Nasopharyngeal Neoplasms / pathology
  • Nasopharyngeal Neoplasms / therapy*
  • Receptor, Notch1 / genetics
  • Xenograft Model Antitumor Assays

Substances

  • Epstein-Barr Virus Nuclear Antigens
  • Intracellular Signaling Peptides and Proteins
  • MIRN31 microRNA, human
  • MicroRNAs
  • Receptor, Notch1
  • WDR5 protein, human
  • Histone-Lysine N-Methyltransferase
  • EBV-encoded nuclear antigen 1