A 4-Year Observational Clinical Study of 24 Adult Pompe Disease Patients under Alglucosidase Alfa Enzyme Replacement Therapy
J Neuromuscul Dis
.
2015;2(s1):S69.
Authors
Karolina M Stepien
1
,
Jane Whitby
1
,
Mark Roberts
1
,
Reena Sharma
1
Affiliation
1
The Mark Holland Metabolic Unit, Salford Royal Hospital NHS Foundation Trust, Salford, UK.
PMID:
27858656
No abstract available