Lentiviral Stem Cell Gene Therapy for Pompe Disease
J Neuromuscul Dis
.
2015;2(s1):S64.
Authors
Qiushi Liang
1
,
Merel Stok
2
,
Yvette van Helsdingen
1
,
Guus van der Velden
1
,
Ed Jacobs
3
,
Dirk Duncker
4
,
Arnold Reuser
2
,
Ans van der Ploeg
2
,
Arnold Vulto
5
,
Niek P van Til
1
,
Gerard Wagemaker
6
Affiliations
1
Department of Hematology, Erasmus MC University Medical Center, Rotterdam, Netherlands.
2
Center for Lysosomal and Metabolic Diseases & Department of Clinical Genetics, Erasmus MC University Medical Center, Rotterdam, Netherlands.
3
Department of Genetics, Erasmus MC University Medical Center, Rotterdam, Netherlands.
4
Department of Experimental Cardiology, Erasmus MC University Medical Center, Rotterdam, Netherlands.
5
Hospital Pharmacy, Erasmus MC University Medical Center, Rotterdam, Netherlands.
6
Hacettepe University, Stem Cell Research and Development Center, Ankara, Turkey.
PMID:
27858653
No abstract available