The Pompe Registry: 10 Years of Data

Affiliations

• ¹ Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC, USA.
• ² National Taiwan University Hospital, Taipei, Taiwan.
• ³ Department of Medical Genetics, Fernandes Figueira Institute, FIOCRUZ, Rio de Janeiro, Brazil.
• ⁴ Genzyme, a Sanofi company, Cambridge, MA, USA.
• ⁵ Department of Pediatrics & Center for Lysosomal and Metabolic Diseases, Erasmus MC University Medical Center, Rotterdam, Netherlands.