Long-term use of pegfilgrastim in children with severe congenital neutropenia: clinical and pharmacokinetic data

Blood. 2016 Oct 27;128(17):2178-2181. doi: 10.1182/blood-2016-07-727891. Epub 2016 Sep 12.
No abstract available

Publication types

  • Letter

MeSH terms

  • Adolescent
  • Child
  • Child, Preschool
  • Cohort Studies
  • Congenital Bone Marrow Failure Syndromes
  • Female
  • Filgrastim / pharmacokinetics*
  • Filgrastim / therapeutic use*
  • Granulocyte Colony-Stimulating Factor / administration & dosage
  • Granulocyte Colony-Stimulating Factor / pharmacokinetics
  • Humans
  • Male
  • Neutropenia / congenital*
  • Neutropenia / drug therapy
  • Neutropenia / metabolism
  • Polyethylene Glycols / pharmacokinetics*
  • Polyethylene Glycols / therapeutic use*
  • Time Factors
  • Treatment Outcome

Substances

  • Granulocyte Colony-Stimulating Factor
  • pegfilgrastim
  • Polyethylene Glycols
  • Filgrastim

Supplementary concepts

  • Neutropenia, Severe Congenital, Autosomal Recessive 3