1 Division of Genetics and Genomics, Boston Children's Hospital, Boston, MA 02115, USA ; Department of Pediatrics and Genetics, Harvard Medical School, Boston, MA 02115, USA ; The Stem Cell Program, Boston Children's Hospital, Boston, MA 02115, USA.
2 Departamento de Neurología, Escuela de Medicina, Pontificia Universidad Catolica de Chile, Santiago 8330033, Chile.
3 Department of Geriatric Medicine, Tokyo Metropolitan Institute of Gerontology, Tokyo 173-0015, Japan.