Gene Therapy for Blinding Pediatric Eye Disorders

Adv Pediatr. 2015 Aug;62(1):185-210. doi: 10.1016/j.yapd.2015.04.012.
No abstract available

Keywords: Gene replacement therapy; Inherited eye disorders; Ocular disorders.

Publication types

  • Review

MeSH terms

  • Child
  • Eye Diseases / genetics
  • Eye Diseases / therapy*
  • Genetic Therapy / methods*
  • Humans
  • Treatment Outcome