3,4-Dihydro-1,3,5-triazin-2(1H)-ones as the First Dual BACE-1/GSK-3β Fragment Hits against Alzheimer's Disease

ACS Chem Neurosci. 2015 Oct 21;6(10):1665-82. doi: 10.1021/acschemneuro.5b00121. Epub 2015 Aug 3.

Abstract

One of the main obstacles toward the discovery of effective anti-Alzheimer drugs is the multifactorial nature of its etiopathology. Therefore, the use of multitarget-directed ligands has emerged as particularly suitable. Such ligands, able to modulate different neurodegenerative pathways, for example, amyloid and tau cascades, as well as cognitive and neurogenic functions, are fostered to come. In this respect, we report herein on the first class of BACE-1/GSK-3β dual inhibitors based on a 3,4-dihydro-1,3,5-triazin-2(1H)-one skeleton, whose hit compound 1 showed interesting properties in a preliminary investigation. Notably, compound 2, endowed with well-balanced potencies against the two isolated enzymes (IC50 of 16 and 7 μM against BACE-1 and GSK-3β, respectively), displayed effective neuroprotective and neurogenic activities and no neurotoxicity in cell-based assays. It also showed good brain permeability in a pharmacokinetic assessment in mice. Overall, triazinone derivatives, thanks to the simultaneous modulation of multiple points of the diseased network, might emerge as suitable candidates to be tested in in vivo Alzheimer's disease models.

Keywords: 6-amino-3,4-dihydro-1,3,5-triazin-2(1H)-one; Alzheimer’s disease; drug design; glycogen-synthase kinase-3β; multitarget drug discovery; multitarget-directed ligands; β-secretase.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Amyloid Precursor Protein Secretases / metabolism*
  • Amyloid beta-Protein Precursor / genetics
  • Amyloid beta-Protein Precursor / metabolism
  • Animals
  • Animals, Newborn
  • Antipsychotic Agents / chemistry*
  • Antipsychotic Agents / pharmacology*
  • Aspartic Acid Endopeptidases / metabolism*
  • Cells, Cultured
  • Cerebral Cortex / cytology
  • Glioma / pathology
  • Glycogen Synthase Kinase 3 / metabolism*
  • Glycogen Synthase Kinase 3 beta
  • Humans
  • Inhibitory Concentration 50
  • Lipopolysaccharides / pharmacology
  • Mice
  • Neuroglia / drug effects
  • Rats
  • Rats, Wistar
  • Time Factors
  • Triazines / chemistry
  • Triazines / pharmacology
  • Triazines / therapeutic use*
  • Tubulin / metabolism

Substances

  • Amyloid beta-Protein Precursor
  • Antipsychotic Agents
  • Lipopolysaccharides
  • Triazines
  • Tubulin
  • GSK3B protein, human
  • Glycogen Synthase Kinase 3 beta
  • Gsk3b protein, mouse
  • Gsk3b protein, rat
  • Glycogen Synthase Kinase 3
  • Amyloid Precursor Protein Secretases
  • Aspartic Acid Endopeptidases
  • Bace1 protein, rat