The holy grail of cystic fibrosis research: pharmacological repair of the F508del-CFTR mutation

Ann Transl Med. 2015 May;3(Suppl 1):S24. doi: 10.3978/j.issn.2305-5839.2015.02.32.

¹ 1 European Institute for Research in Cystic Fibrosis, San Raffaele Scientific Institute, Milan, Italy ; 2 SCDU of Pediatrics, Department of Health Sciences, University of Piemonte Orientale, Novara, Italy ; 3 Regional Cystic Fibrosis Center; Pediatric Unit, Department of Translational Medical Sciences, Federico II University, Naples, Italy ; 4 Equipe 11 labellisee Ligue contre le Cancer; INSERM U1138; Centre de Recherche des Cordeliers, Paris, France ; 5 Universite Paris Descartes, Paris, France ; 6 Metabolomics and Cell Biology Platforms, Institut Gustave Roussy, Villejuif, France ; 7 Pole de Biologie, Hopital Européen Georges Pompidou, AP-HP, Paris, France.

No abstract available