Potentiators for cystic fibrosis - targeting the underlying molecular defect

Paediatr Respir Rev. 2015 Jun;16(3):162-4. doi: 10.1016/j.prrv.2015.04.003. Epub 2015 Apr 20.
No abstract available

Publication types

  • Review

MeSH terms

  • Adult
  • Aminophenols / adverse effects
  • Aminophenols / therapeutic use*
  • Child
  • Child, Preschool
  • Chloride Channel Agonists / adverse effects
  • Chloride Channel Agonists / therapeutic use*
  • Cystic Fibrosis / drug therapy
  • Cystic Fibrosis / genetics*
  • Cystic Fibrosis Transmembrane Conductance Regulator / genetics*
  • Humans
  • Mutation
  • Quinolones / adverse effects
  • Quinolones / therapeutic use*
  • Respiratory Function Tests

Substances

  • Aminophenols
  • Chloride Channel Agonists
  • Quinolones
  • Cystic Fibrosis Transmembrane Conductance Regulator
  • ivacaftor