Oligonucleotide therapies: the future of amyotrophic lateral sclerosis treatment?

Neurodegener Dis Manag. 2015;5(2):93-5. doi: 10.2217/nmt.15.4.
No abstract available

Keywords: C9orf72; SOD1; amyotrophic lateral sclerosis; frontotemporal dementia; oligonucleotides ASO.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Amyotrophic Lateral Sclerosis / genetics
  • Amyotrophic Lateral Sclerosis / therapy*
  • Animals
  • C9orf72 Protein
  • Genetic Therapy / methods
  • Humans
  • Oligonucleotides / therapeutic use*
  • Proteins / genetics
  • Superoxide Dismutase / genetics
  • Superoxide Dismutase-1

Substances

  • C9orf72 Protein
  • C9orf72 protein, human
  • Oligonucleotides
  • Proteins
  • SOD1 protein, human
  • Superoxide Dismutase
  • Superoxide Dismutase-1