Targeted inhibition of osteosarcoma tumor growth by bone marrow-derived mesenchymal stem cells expressing cytosine deaminase/5-fluorocytosine in tumor-bearing mice

J Gene Med. 2015 Mar-May;17(3-5):87-99. doi: 10.1002/jgm.2826.

Abstract

Background: Mesenchymal stem cells (MSCs) are considered as an attractive approach for gene or drug delivery in cancer therapy. In the present study, the ability of human bone marrow-derived MSCs expressing the cytosine deaminase/5-fluorocytosine prodrug (CD/5-FC MSCs) to target the human osteosarcoma cell line Cal72 was evaluated.

Methods: The stable CD/5-FC MSC cell line was established by transfection of pEGFP containing the cytosine deaminase gene into MSCs with G418 selection. The anti-tumor effect was verified by a bystander effect assay in vitro and co-injection of Cal72 and CD/5-FC MSCs in cancer-bearing mice.

Results: The therapeutic CD/5-FC MSCs retained the characteristics of multipotent cells, such as differentiation into adipocytes/osteocytes and expression of mesenchymal markers (CD90 and CD44), and showed migration toward Cal72 cells to a greater extent than the native MSCs. The bystander effect assay showed that the CD/5-FC MSCs significantly augmented Cal72 cytotoxicity in direct co-culture and in the presence of 5-FC through the application of conditioned medium. In osteosarcoma-bearing mice, the CD/5-FC MSCs inhibited tumor growth compared to control mice subcutaneously injected with only Cal72 cells.

Conclusions: Taken together, these findings suggest that CD/5-FC MSCs may be suitable for targeting human osteosarcoma.

Keywords: bystander effect; cytosine deaminase; mesenchymal stem cell; osteosarcoma; prodrug; tumor tropism.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Bone Marrow Cells / cytology*
  • Bone Marrow Cells / drug effects
  • Bystander Effect / drug effects
  • Cell Death / drug effects
  • Cell Line, Tumor
  • Cell Proliferation / drug effects
  • Cell Separation
  • Cell Survival / drug effects
  • Cytosine Deaminase / metabolism*
  • Female
  • Flucytosine / therapeutic use*
  • Genes, Transgenic, Suicide
  • Mesenchymal Stem Cell Transplantation*
  • Mesenchymal Stem Cells / cytology*
  • Mesenchymal Stem Cells / drug effects
  • Mice, Nude
  • Osteosarcoma / drug therapy
  • Osteosarcoma / pathology*
  • Osteosarcoma / therapy*
  • Phytochemicals / pharmacology
  • Transgenes

Substances

  • Phytochemicals
  • Flucytosine
  • Cytosine Deaminase