Familial amyloidosis: great progress for an orphan disease

J Hepatol. 2015 Feb;62(2):483-5. doi: 10.1016/j.jhep.2014.09.008. Epub 2014 Sep 16.
No abstract available

Keywords: Familial amyloidosis; Liver transplantation; Pharmacological therapy; Tafamidis.

Publication types

  • Review

MeSH terms

  • Amyloidosis, Familial* / diagnosis
  • Amyloidosis, Familial* / epidemiology
  • Amyloidosis, Familial* / therapy
  • Disease Management*
  • Global Health
  • Humans
  • Morbidity
  • Rare Diseases*