Applications of Biophysics in High-Throughput Screening Hit Validation

J Biomol Screen. 2014 Jun;19(5):707-14. doi: 10.1177/1087057114529462. Epub 2014 Apr 2.

Abstract

For approximately a decade, biophysical methods have been used to validate positive hits selected from high-throughput screening (HTS) campaigns with the goal to verify binding interactions using label-free assays. By applying label-free readouts, screen artifacts created by compound interference and fluorescence are discovered, enabling further characterization of the hits for their target specificity and selectivity. The use of several biophysical methods to extract this type of high-content information is required to prevent the promotion of false positives to the next level of hit validation and to select the best candidates for further chemical optimization. The typical technologies applied in this arena include dynamic light scattering, turbidometry, resonance waveguide, surface plasmon resonance, differential scanning fluorimetry, mass spectrometry, and others. Each technology can provide different types of information to enable the characterization of the binding interaction. Thus, these technologies can be incorporated in a hit-validation strategy not only according to the profile of chemical matter that is desired by the medicinal chemists, but also in a manner that is in agreement with the target protein's amenability to the screening format. Here, we present the results of screening strategies using biophysics with the objective to evaluate the approaches, discuss the advantages and challenges, and summarize the benefits in reference to lead discovery. In summary, the biophysics screens presented here demonstrated various hit rates from a list of ~2000 preselected, IC50-validated hits from HTS (an IC50 is the inhibitor concentration at which 50% inhibition of activity is observed). There are several lessons learned from these biophysical screens, which will be discussed in this article.

Keywords: differential scanning fluorimetry; dynamic light scattering; resonance waveguide; surface plasmon resonance; turbidometry.

MeSH terms

  • Biological Assay
  • Biophysics / methods*
  • Drug Design
  • Drug Discovery / methods*
  • Epigenomics
  • Fluorescence Resonance Energy Transfer
  • Fluorometry
  • High-Throughput Screening Assays / methods*
  • Inhibitory Concentration 50
  • Kinetics
  • Light
  • Magnetic Resonance Spectroscopy
  • Molecular Weight
  • Nephelometry and Turbidimetry
  • Scattering, Radiation
  • Small Molecule Libraries / chemistry*
  • Structure-Activity Relationship
  • Surface Plasmon Resonance

Substances

  • Small Molecule Libraries