Optimizing treatments in rare diseases: will our evidence come from registry data?

Leuk Res. 2014 Apr;38(4):421-2. doi: 10.1016/j.leukres.2014.01.015. Epub 2014 Feb 6.
No abstract available

Publication types

  • Editorial
  • Comment

MeSH terms

  • Antimetabolites, Antineoplastic / therapeutic use*
  • Azacitidine / therapeutic use*
  • Female
  • Humans
  • Leukemia, Myelomonocytic, Chronic / drug therapy*
  • Leukemia, Myelomonocytic, Chronic / mortality*
  • Male

Substances

  • Antimetabolites, Antineoplastic
  • Azacitidine