Genetics. GWAS to therapy by genome edits?

Science. 2013 Oct 11;342(6155):206-7. doi: 10.1126/science.1245813.
No abstract available

Publication types

  • Research Support, N.I.H., Extramural
  • Comment

MeSH terms

  • Animals
  • Carrier Proteins / genetics*
  • Enhancer Elements, Genetic*
  • Erythroid Cells / metabolism*
  • Fetal Hemoglobin / biosynthesis*
  • Gene Expression Regulation*
  • Hemoglobinopathies / genetics*
  • Humans
  • Nuclear Proteins / genetics*
  • Repressor Proteins

Substances

  • BCL11A protein, human
  • Carrier Proteins
  • Nuclear Proteins
  • Repressor Proteins
  • Fetal Hemoglobin