No abstract available
MeSH terms
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2-Hydroxypropyl-beta-cyclodextrin
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Contraindications
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Drug Compounding
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Evoked Potentials, Auditory, Brain Stem / drug effects
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Female
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Humans
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Infant
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Infusions, Intravenous
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Injections, Spinal
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Niemann-Pick Disease, Type C / drug therapy*
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Orphan Drug Production
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beta-Cyclodextrins / administration & dosage
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beta-Cyclodextrins / therapeutic use*
Substances
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beta-Cyclodextrins
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2-Hydroxypropyl-beta-cyclodextrin