Two new drugs for homozygous familial hypercholesterolemia: managing benefits and risks in a rare disorder

MeSH terms

• Anticholesteremic Agents / administration & dosage*
• Anticholesteremic Agents / adverse effects*
• Anticholesteremic Agents / economics
• Benzimidazoles / administration & dosage
• Benzimidazoles / adverse effects
• Benzimidazoles / economics
• Cholesterol, LDL / blood
• Drug Approval
• Fatty Liver / chemically induced
• Humans
• Hyperlipoproteinemia Type II / drug therapy*
• Oligonucleotides / administration & dosage
• Oligonucleotides / adverse effects
• Oligonucleotides / economics
• Product Surveillance, Postmarketing
• Rare Diseases / drug therapy
• United States
• United States Food and Drug Administration