Gene therapy for Canavan's disease takes a step forward

Mol Ther. 2013 Mar;21(3):505-6. doi: 10.1038/mt.2013.25.
No abstract available

MeSH terms

  • Amidohydrolases / genetics
  • Amidohydrolases / metabolism
  • Aspartic Acid / analogs & derivatives
  • Aspartic Acid / metabolism
  • Canavan Disease / genetics
  • Canavan Disease / therapy*
  • Dependovirus* / genetics
  • Genetic Therapy / methods*
  • Genetic Vectors*
  • Humans
  • Recombination, Genetic

Substances

  • Aspartic Acid
  • N-acetylaspartate
  • Amidohydrolases
  • aspartoacylase