Structural basis for inhibiting β-amyloid oligomerization by a non-coded β-breaker-substituted endomorphin analogue

ACS Chem Biol. 2011 Nov 18;6(11):1265-76. doi: 10.1021/cb200103h. Epub 2011 Sep 19.

Abstract

The distribution of endomorphins (EM) 1 and 2 in the human brain inversely correlates with cerebral neurodegeneration in Alzheimer's disease (AD), implying a protective role. These endogenous opioid peptides incorporate aromatic residues and a β-breaker motif, as seen in several optimized inhibitors of Aβ aggregation. The activity of native endomorphins was studied, as well as the rationally designed analogue Aib-1, which includes a remarkably efficient β-breaker, α-aminoisobutyric acid (Aib). In vitro and GFP fusion protein assays showed that Aib-1 interacted with Aβ and markedly inhibited the formation of toxic oligomer and fibril growth. Moreover, Aib-1 prevented the toxicity of Aβ toward neuronal PC12 cells and markedly rectified reduced longevity of an AD fly model. Atomistic simulations and NMR-derived solution structures revealed that Aib-1 significantly reduced the propensity of Aβ to aggregate due to multimode interactions including aromatic, hydrophobic, and polar contacts. We suggest that hindering the self-assembly process by interfering with the aromatic core of amyloidogenic peptides may pave the way toward developing therapeutic agents to treat amyloid-associated diseases.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Amyloid beta-Peptides / chemistry*
  • Amyloid beta-Peptides / metabolism
  • Animals
  • Biological Products / chemistry
  • Biological Products / pharmacology
  • Cell Survival / drug effects
  • Cells, Cultured
  • Dose-Response Relationship, Drug
  • Drosophila melanogaster / drug effects
  • Female
  • Magnetic Resonance Spectroscopy
  • Models, Molecular
  • Molecular Structure
  • Oligopeptides / chemistry*
  • Oligopeptides / pharmacology*
  • PC12 Cells
  • Peptide Fragments / chemistry*
  • Peptide Fragments / metabolism
  • Protein Multimerization / drug effects*
  • Protein Stability
  • Rats
  • Structure-Activity Relationship

Substances

  • Amyloid beta-Peptides
  • Biological Products
  • Oligopeptides
  • Peptide Fragments
  • amyloid beta-protein (1-42)
  • endomorphin 1
  • endomorphin 2