Mechanistic studies of peptide self-assembly: transient α-helices to stable β-sheets

J Am Chem Soc. 2010 Dec 29;132(51):18223-32. doi: 10.1021/ja1069882. Epub 2010 Dec 7.

Abstract

The pathologic self-assembly of proteins is associated with typically late-onset disorders such as Alzheimer's disease, Parkinson's disease, and type 2 diabetes. Important mechanistic details of the self-assembly are unknown, but there is increasing evidence supporting the role of transient α-helices in the early events. Islet amyloid polypeptide (IAPP) is a 37-residue polypeptide that self-assembles into aggregates that are toxic to the insulin-producing β cells. To elucidate early events in the self-assembly of IAPP, we used limited proteolysis to identify an exposed and flexible region in IAPP monomer. This region includes position 20 where a serine-to-glycine substitution (S20G) is associated with enhanced formation of amyloid fibrils and early onset type 2 diabetes. To perform detailed biophysical studies of the exposed and flexible region, we synthesized three peptides including IAPP(11-25)WT (wild type), IAPP(11-25)S20G, and IAPP(11-25)S20P. Solution-state NMR shows that all three peptides transiently populate the α-helical conformational space, but the S20P peptide, which does not self-assemble, transiently samples a broken helix. Under similar sample conditions, the WT and S20G peptides populate the α-helical intermediate state and β-sheet end state, respectively, of fibril formation. Our results suggest a mechanism for self-assembly that includes the stabilization of transient α-helices through the formation of NMR-invisible helical intermediates followed by an α-helix to β-sheet conformational rearrangement. Furthermore, our results suggest that reducing intermolecular helix-helix contacts as in the S20P peptide is an attractive strategy for the design of blockers of peptide self-assembly.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Amino Acid Substitution
  • Glycine / chemistry
  • Humans
  • Islet Amyloid Polypeptide / antagonists & inhibitors
  • Islet Amyloid Polypeptide / chemical synthesis
  • Islet Amyloid Polypeptide / chemistry*
  • Nuclear Magnetic Resonance, Biomolecular
  • Proline / chemistry
  • Protein Structure, Secondary
  • Serine / chemistry

Substances

  • Islet Amyloid Polypeptide
  • Serine
  • Proline
  • Glycine