Telomerase inhibitors for the treatment of brain tumors and the potential of intranasal delivery

Curr Opin Mol Ther. 2010 Apr;12(2):168-75.

Abstract

A fundamental limitation in the treatment of brain tumors is that < 1% of most therapeutic agents administered systemically are able to cross the blood-brain barrier (BBB). The development of new strategies that circumvent the BBB should increase the likelihood of tumor response to selected therapeutic agents. Intranasal delivery (IND) is a practical, noninvasive method of bypassing the BBB to deliver therapeutic agents to the brain. This technique has demonstrated promising results in the treatment of neurological disorders. Telomerase is a reverse transcriptase that is expressed in the vast majority of malignant gliomas, although not in the healthy brain. Telomerase inhibition can therefore be used as a therapeutic strategy for selectively targeting malignant gliomas. The first successful IND of a telomerase inhibitor as a therapy for brain tumors was GRN-163, an oligonucleotide N3'-->5' thiophosphoramidate telomerase inhibitor, which was successfully administered into intracerebral tumors in rats with no apparent toxicity. GRN-163 exhibited favorable tumor uptake and inhibited tumor growth, leading to prolonged lifespan in treated animals. The IND of telomerase inhibitors represents a new therapeutic approach that appears to selectively kill tumor cells, without inducing toxic effects in the surrounding healthy brain tissue.

Publication types

  • Review

MeSH terms

  • Administration, Intranasal
  • Animals
  • Blood-Brain Barrier / physiology
  • Brain Neoplasms / drug therapy*
  • Enzyme Inhibitors* / administration & dosage
  • Enzyme Inhibitors* / chemistry
  • Enzyme Inhibitors* / therapeutic use
  • Humans
  • Indoles / administration & dosage
  • Indoles / chemistry
  • Indoles / metabolism
  • Indoles / therapeutic use
  • Neoplasms / enzymology
  • Neoplasms / genetics
  • Neural Pathways / anatomy & histology
  • Niacinamide / administration & dosage
  • Niacinamide / analogs & derivatives
  • Niacinamide / chemistry
  • Niacinamide / metabolism
  • Niacinamide / therapeutic use
  • Oligonucleotides / administration & dosage
  • Oligonucleotides / chemistry
  • Oligonucleotides / metabolism
  • Oligonucleotides / therapeutic use
  • Telomerase / antagonists & inhibitors*

Substances

  • Enzyme Inhibitors
  • GRN163
  • Indoles
  • Oligonucleotides
  • Niacinamide
  • Telomerase
  • imetelstat