The development of antisense oligonucleotide therapies for Duchenne muscular dystrophy: report on a TREAT-NMD workshop hosted by the European Medicines Agency (EMA), on September 25th 2009

Neuromuscul Disord. 2010 May;20(5):355-62. doi: 10.1016/j.nmd.2010.03.005. Epub 2010 Mar 26.
No abstract available

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Biological Therapy
  • Europe
  • Genetic Therapy
  • Guidelines as Topic
  • Humans
  • Muscular Dystrophy, Duchenne / therapy*
  • Oligonucleotides, Antisense / chemistry
  • Oligonucleotides, Antisense / therapeutic use*
  • Outcome Assessment, Health Care

Substances

  • Oligonucleotides, Antisense