Lysosomal storage diseases: new challenges

Acta Paediatr. 2008 Apr;97(457):5-6. doi: 10.1111/j.1651-2227.2008.00645.x.
No abstract available

Publication types

  • Introductory Journal Article

MeSH terms

  • Animals
  • Disease Models, Animal
  • Genetic Therapy
  • Lysosomal Storage Diseases / physiopathology
  • Lysosomal Storage Diseases / therapy*