No abstract available
MeSH terms
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Animals
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Central Nervous System Diseases / genetics
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Central Nervous System Diseases / therapy*
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Disease Models, Animal
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Gene Expression Regulation / genetics
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Gene Targeting / methods*
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Genetic Vectors / genetics
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Heredodegenerative Disorders, Nervous System / genetics
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Heredodegenerative Disorders, Nervous System / therapy*
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Humans
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MicroRNAs / genetics
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Oligonucleotides, Antisense / genetics
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RNA, Messenger / genetics
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RNA, Small Interfering / genetics
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Treatment Outcome
Substances
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MicroRNAs
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Oligonucleotides, Antisense
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RNA, Messenger
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RNA, Small Interfering