Gene-targeted therapies for the central nervous system

Arch Neurol. 2008 Apr;65(4):447-51. doi: 10.1001/archneur.65.4.nnr70007. Epub 2008 Feb 11.
No abstract available

Publication types

  • Review

MeSH terms

  • Animals
  • Central Nervous System Diseases / genetics
  • Central Nervous System Diseases / therapy*
  • Disease Models, Animal
  • Gene Expression Regulation / genetics
  • Gene Targeting / methods*
  • Genetic Vectors / genetics
  • Heredodegenerative Disorders, Nervous System / genetics
  • Heredodegenerative Disorders, Nervous System / therapy*
  • Humans
  • MicroRNAs / genetics
  • Oligonucleotides, Antisense / genetics
  • RNA, Messenger / genetics
  • RNA, Small Interfering / genetics
  • Treatment Outcome

Substances

  • MicroRNAs
  • Oligonucleotides, Antisense
  • RNA, Messenger
  • RNA, Small Interfering