Direct diagnosis of Wilson disease by molecular genetics

J Pediatr. 2006 Jan;148(1):138-40. doi: 10.1016/j.jpeds.2005.07.036.

Abstract

In 3 children with chronic liver disease, although multiple studies of copper metabolism were normal, which made the diagnosis of Wilson disease unlikely, analysis of ATP7B gene showed disease causing mutations in all. Molecular diagnosis should be considered in children with enigmatic liver disease, especially those with features of nonalcoholic fatty liver disease.

Publication types

  • Case Reports

MeSH terms

  • Adenosine Triphosphatases / genetics*
  • Adolescent
  • Antidotes / therapeutic use
  • Cation Transport Proteins / genetics*
  • Child
  • Copper-Transporting ATPases
  • Female
  • Hepatolenticular Degeneration / diagnosis*
  • Hepatolenticular Degeneration / drug therapy
  • Hepatolenticular Degeneration / genetics
  • Humans
  • Male
  • Mutation*
  • Mutation, Missense
  • Penicillamine / therapeutic use
  • Retrospective Studies
  • Sequence Deletion
  • Treatment Outcome

Substances

  • Antidotes
  • Cation Transport Proteins
  • Adenosine Triphosphatases
  • ATP7B protein, human
  • Copper-Transporting ATPases
  • Penicillamine